Newborn Genetic Screening for Spinal Muscular AtrophySpinal muscular atrophy (SMA) is a rare genetic condition that causes muscle weakness. SMA is caused by a mistake in a specific gene. People with the faulty gene are not... By Editorial Team 3 min readBookmark for laterReactions 0 reactions Comments0 comments
Comparing Spinraza and Evrysdi: Things to ConsiderIf you are taking Spinraza® (nusinersen) for spinal muscular atrophy (SMA), then you may be curious about Evrysdi® (risdiplam). Both therapies are available in the United States, but there are... By Editorial Team 2 min readBookmark for laterReactions 0 reactions Comments0 comments
What Does It Mean to Be a Silent Carrier for SMA?Spinal muscular atrophy (SMA) is a rare genetic disorder passed from parents to their children. SMA affects the spinal nerves by causing them to waste away. This results in the... By Editorial Team 3 min readBookmark for laterReactions 0 reactions Comments0 comments
Clinical Trial GlossaryClinical trials have a language of their own. It helps to understand the common terms used when describing a clinical trial before you sign up. Here are some of the... By Editorial Team 4 min readBookmark for laterReactions 0 reactions Comments0 comments
Clinical Trial ParticipationClinical trials are medical studies that pose a question: Does a new treatment work better than older treatments? Each year, thousands of treatments are tested in controlled experiments called clinical... By Editorial Team 4 min readBookmark for laterReactions 0 reactions Comments0 comments
Understanding Clinical TrialsA clinical trial is a type of research. Research is the process scientists use to explain how our bodies work or why our bodies stop working well. Clinical trials are... By Editorial Team 4 min readBookmark for laterReactions 0 reactions Comments0 comments