Newborn Genetic Screening for Spinal Muscular AtrophySpinal muscular atrophy (SMA) is a rare genetic condition that causes muscle weakness. SMA is caused by a mistake in a specific gene. People with the faulty gene are not... By Editorial TeamBookmark for later Reactions 0 reactions Comments0 comments
Comparing Spinraza® and Evrysdi®: Things to ConsiderIf you are taking Spinraza® (nusinersen) for spinal muscular atrophy (SMA), then you may be curious about Evrysdi® (risdiplam). Both therapies are available in the United States, but there are... By Editorial TeamBookmark for later Reactions 0 reactions Comments0 comments
What Does It Mean to Be a Silent Carrier for SMA?Spinal muscular atrophy (SMA) is a rare genetic disorder passed from parents to their children. SMA affects the spinal nerves by causing them to waste away. This results in the... By Editorial TeamBookmark for later Reactions 0 reactions Comments0 comments
Clinical Trial GlossaryClinical trials have a language of their own. It helps to understand the common terms used when describing a clinical trial before you sign up. Here are some of the... By Editorial TeamBookmark for later Reactions 0 reactions Comments0 comments
Clinical Trial ParticipationClinical trials are medical studies that pose a question: Does a new treatment work better than older treatments? Each year, thousands of treatments are tested in controlled experiments called clinical... By Editorial TeamBookmark for later Reactions 0 reactions Comments0 comments
Understanding Clinical TrialsA clinical trial is a type of research. Research is the process scientists use to explain how our bodies work or why our bodies stop working well. Clinical trials are... By Editorial TeamBookmark for later Reactions 0 reactions Comments0 comments
